Our 2nd Annual MDF Gala was a tremendous success, thanks to the many heroes in our special myotonic dystrophy (DM) community. More than 250 guests celebrated MDF’s progress since its first gala in 2013, raising $500,000 to drive the next phase of our Care and a Cure mission for families living with myotonic dystrophy.
Jazzy Wright joined MDF in October 2016 as the organization’s Communications Manager. Jazzy will also manage the MDF communications strategy, and produce all internal and external communications pieces for the organization.
This year’s event was the best and biggest yet! Click here to learn about all that was accomplished when we came together in Washington, DC.
Congratulations to our Community Leadership Award winners: Loraine Dressler, Carolyn Valek and Eric & Taylor Jensen! Click here to learn more about the amazing work they do for Care and a Cure.
MDF held the first myotonic dystrophy Patient-Focused Drug Development meeting with key senior leadership from the Food and Drug Administration (FDA) as part of the 2016 MDF Annual Conference. We designed the meeting to build on the work MDF has been conducting with the FDA to define and optimize the regulatory pathway for potential DM therapies. The meeting, the first Externally-Led PFDD meeting and the largest PFDD meeting held to date with over 200 attendees in the room and online, is helping change the way the FDA understands DM, the DM community and the approach to regulatory review for DM therapies.