Researchers at the University of Florida, led by Dr. Tetsuo Ashizawa, recently published a study in which they developed a strategy for DM1 stem cell therapy involving gene modification.
Researchers and medical professionals from Europe, Canada and the USA gathered recently for a workshop in Europe to identify the main respiratory issues and best respiratory treatments for people with DM.
As a clinician and researcher, Dr. Benedikt Schoser of Ludwig-Maximilians University of Munich, Germany, is focused on how research findings can be translated into improved patient care - and how patient concerns can help guide researchers to new areas of interest.
To support myotonic dystrophy drug development efforts, MDF held a science workshop in September 2014 at our annual conference. The workshop brought together more than 50 DM researchers and industry representatives from around the world to review where we are in the development of clinical trial endpoint measures for DM.
As part of MDF's countdown to the IDMC-10, we are introducing you to some of the international DM researchers who will attend the conference. Meet Dr. Bé Wieringa, MDF Lifetime Achievement awardee and leading investigator.