New fly models show a DM2 phenotype at least as severe as DM1 and may provide a platform for studies of genetic modifiers and candidate therapy screening in DM.
A large retrospective study helps clarify genotype-cardiac phenotype relationships in adult DM1.
A recent review article makes the case that DM is a brain disease and that better understanding of and treatment strategies for the neurological consequences of DM are essential.
MDF strives to help National Institutes of Health (NIH) grant applicants compete for research funding.
Taking as many shots on goal as possible is the only path to approval and reimbursement of safe and effective drugs for DM.