Home / Patients Family / Academy / Digital Academy

Digital Academy

 

MDF community members living with DM and their caregivers present on current symptom management strategies for living with DM, and what they would like to see in clinically-meaningful therapies. Dr. Jonathan Goldsmith, M.D., FACP, head of the Office of Rare Diseases at the FDA, provided a summary of the proceedings and what the FDA took away from the patient input shared at this meeting – at the 2016 DM Patient-Focused Drug Development meeting, a component of the 2016 MDF Annual Conference.

 

MDF community members living with DM, and their caregivers present on the impacts of DM on daily living, in response to specific questions posed by the Food and Drug Administration, which is in charge of reviewing and approving therapies in the U.S. Dr. Janet Woodcock, M.D., who leads all drug evaluation and research at the FDA, also provided remarks – at the 2016 DM Patient-Focused Drug Development meeting, a component of the 2016 MDF Annual Conference.

 

MDF Chief Executive Officer Molly White provides a look back at the first 10 years of MDF programming and research progress, and the significant accomplishments achieved – at the 2016 MDF Annual Conference.

This webinar is essential for meeting attendees and will cover everything you need to know to make an impact on the FDA.

Patient Focused Drug Development (PFDD) meeting: This year at our annual conference MDF will host the first community meeting focused on the Food and Drug Administration (FDA). MDF community members will educate the FDA and other federal agency representatives about symptoms and disease issues that are most important to patients and families, and guide their thinking on DM drug review. The FDA wants to understand which benefits patients seek from therapies and what risks they might be willing to accept to gain specific benefits.

Watch this webinar for tips and guidance on how to be a successful advocate for myotonic dystrophy Care and a Cure on Capital Hill during our 2016 Hill Day Friday, September 16, 2016. Additional training will also be provided starting at 8:30 AM at the 2016 MDF Annual Conference hotel before we board the buses to start Hill Day. Questions? Contact MDF via email or phone: 415-800-7777. 

Partners

© Myotonic Dystrophy Foundation. All rights reserved.