{"id":18893,"date":"2016-09-15T13:00:55","date_gmt":"2016-09-15T20:00:55","guid":{"rendered":"https:\/\/mr66givry2.onrocket.site\/?post_type=events&#038;p=18893"},"modified":"2026-02-13T13:03:37","modified_gmt":"2026-02-13T21:03:37","slug":"2016-mdf-annual-conference-in-washington-dc","status":"publish","type":"events","link":"https:\/\/myotonic.org\/es\/events\/2016-mdf-annual-conference-in-washington-dc\/","title":{"rendered":"2016 MDF Annual Conference in Washington, DC"},"content":{"rendered":"<div id=\"block-bootstrap-aline-page-title\" class=\"block block-core block-page-title-block\">\n<h2><span class=\"field field--name-title field--type-string field--label-hidden\">2016 MDF Annual Conference<\/span><\/h2>\n<\/div>\n<div id=\"block-bootstrap-aline-content\" class=\"block block-system block-system-main-block\">\n<article class=\"node node--type-page node--view-mode-full\" data-history-node-id=\"1429\">\n<div class=\"node__content\">\n<div class=\"clearfix text-formatted field field--name-body field--type-text-with-summary field--label-hidden field__item\">\n<p><img decoding=\"async\" src=\"https:\/\/myotonic.org\/wp-content\/uploads\/1_201620Conference20Header.png\" alt=\"\" \/><\/p>\n<h2>The Latest in Research, Disease Management, Drug Development and more<\/h2>\n<p>This year\u2019s MDF Annual Conference was\u00a0held Thursday, September 15 &#8211; Saturday, September 17, 2016 in Washington, DC.\u00a0We added an extra day to include the first DM Patient-Focused Drug Development (PFDD) meeting, where \u00a0MDF community members educated the FDA and other federal agency representatives about symptoms and disease issues that are most important to patients and families, and guided their thinking on DM drug review.\u00a0The additional day also allowed us to provide more networking and education opportunities. Read a report about the conference\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1538\">here<\/a>.<\/p>\n<h2>Watch Conference Videos and Presentations<\/h2>\n<p>To access presentations and videos from many of the sessions, click on the headers below.<\/p>\n<h2>Questions?<\/h2>\n<p>For more information, contact MDF at\u00a0<a href=\"mailto:info@myotonic.org\">info@myotonic.org<\/a> or by phone at 415-800-7777.<\/p>\n<\/div>\n<div class=\"field field-name-field_accordion_buckets field-type-entity_reference field-labelhidden slidedown\">\n<div class=\"slideitem\">\n<article data-history-node-id=\"1436\">\n<div>\n<div id=\"accordion-1436\" class=\"accordion\">\n<div class=\"accordion-item\">\n<div id=\"node-1436\" class=\"accordion-collapse collapse show\" aria-labelledby=\"heading-1436\" data-bs-parent=\"#accordion-1436\">\n<div class=\"accordion-body\">\n<div class=\"clearfix text-formatted field field--name-body field--type-text-with-summary field--label-hidden field__item\">\n<p>The 2016 Myotonic Annual Conference Community Track included the following sessions below. You&#8217;ll find links for the presentations and videos\u00a0from those sessions linked below if they are available.<\/p>\n<h2>Thursday, September 15, 2016:<\/h2>\n<ul>\n<li><strong>Patient-Focused Drug Development Meeting<\/strong>, Sheraton College Park North, Beltsville, MD\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/node\/1536\">Short meeting report<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1557\">Video, Part 1<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1558\">Video, Part 2<\/a><\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<h2>Friday, September 16, 2016:<\/h2>\n<ul>\n<li><strong>Hill Day Briefing and Mini-Training<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Hill%20Day%20Briefing%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation (pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM101:\u00a0Getting a Handle on the Basics<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM%20101%20SM-%20Getting%20a%20Handle%20on%20the%20Basics%20-%20Sampson%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation (pdf)<\/a>;<\/li>\n<\/ul>\n<\/li>\n<li><strong>Living Long, Living Well: A Current Approach to Palliative Care<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/digital-academy\/living-long-living-well-current-approach-palliative-care\">Webinar<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM &amp; Intimacy: Talking to Your Doctor<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM1%20and%20Intimacy-%20Talking%20to%20your%20Doctor-%20Gagnon%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<h2>Saturday, September 17, 2016:<\/h2>\n<ul>\n<li><strong>Applying for Disability Coverage: Understanding the Social Secuirty Administration Process<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Applying%20for%20Disability%20-%20Melissa%20Spencer%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Spencer\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/slides\/Applying%20for%20Disability-%20Stacy%20Cloyd%20FNL%202016-09.pptx\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Cloyd\u00a0(pdf)<\/a>;\u00a0<a href=\"http:\/\/myotonic.org\/applying-disability-benefits\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM Pulmonary Considerations: Science and Management Strategies<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM%20Pulmonary%20Considerations%20-Lechtzin%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1548\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>Update &#8211; Myotonic 3.0: Accelerating Drug Development<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/MDF%203.0%20Summary%20-%20Porter%20presentation%20-%20FNL%202016-09-12.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM2: Symptoms Overview and Management Strategies<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM2%20Symptoms%20Day%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Day\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM2%20Symptoms-%20Heatwole.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Heatwole\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/DM2%20Symptoms%20Meola%20FNL%202016-09.pptx\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Meola\u00a0(pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM &amp; Exercise: A Panel Discussion<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Exercise%20and%20DM%20-%20Eichinger%20presentation%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>Occupational Therapy: Getting a Grip on Daily Activity<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Getting%20a%20Grip%20OT%20presentation%20-%20Gagnon%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1552\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM &amp; Sexuality: Talking with Your Partner<\/strong>\n<ul>\n<li>Presentation Not Available<\/li>\n<\/ul>\n<\/li>\n<li><strong>Transitioning to Adulthood: Surviving and Thriving<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/TransitioningtoAdulthoodJoAnn%20Simons-%20Transitions%20Presentation%20v2.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1550\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM &amp; the GI Tract: Overview and Symptom Management<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/GITract.pdf\">Presentation\u00a0(pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM2: Research Update<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM2%20Research%20Day%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Day\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM2%20Research-%20Heatwole%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Heatwole\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Meola_DM2%20Research%20update_MDF_2016.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Meola\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM2%20Research%20Sznajder%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Sznajder\u00a0(pdf)<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>DM &amp; Family Planning<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Family%20Planning%20-%20Schindler%20Cohen%20-%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Cohen &amp; Schindler\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Family%20Planning%20-Blakemore%20Slides%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Blakemore\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1551\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>Myotonic Care and a Cure Progress Report<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Care%20and%20a%20Cure%20Update%20-%20White%20FNL%202016-09-14.pdf\" target=\"_blank\" rel=\"noopener\">Presentation\u00a0(pdf)<\/a>;<\/li>\n<\/ul>\n<\/li>\n<li><strong>DM &amp; the Brain: Science and Symptoms<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM1%20CNS%20Features%20-%20Day%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Day\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/DM%20and%20Brain%20Science%20and%20Symptoms%20Moser%20FNL%202016-09.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Moser\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Meola_%20MDF_CNS_2016%20%20(230PM).pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Meola\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/node\/1554\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<li><strong>Early Stage DM Therapy Development Update<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Pfizer%20Update%20-%20Wood%20presentation%202016-09-17.pdf\" target=\"_blank\" rel=\"noopener\">Pfizer Presentation\u00a0(pdf)<\/a>;<\/li>\n<\/ul>\n<\/li>\n<li><strong>DM Clinical Trial Updates<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/IONIS-DMPKRx%20-%20Mignon%202016-09-17.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; Ionis Pharmaceuticals\u00a0(pdf)<\/a>;\u00a0<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/Horrigan%20-%20AMO%20Pharma%20Tideglusib%20001%20Study%20-%20MDF%20conference%20-%20September%202016%20-%20v3.pdf\" target=\"_blank\" rel=\"noopener\">Presentation &#8211; AMO Pharma\u00a0(pdf)<\/a>;<\/li>\n<\/ul>\n<\/li>\n<li><strong>DM Heroes<\/strong>\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/digital-academy\/dm-heroes\" target=\"_blank\" rel=\"noopener\">Video<\/a><\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<h2>Questions?<\/h2>\n<p>Contact Myotonic\u00a0at\u00a0(415) 872-7924 or via\u00a0<a href=\"mailto:info@myotonic.org?subject=Question%20regarding%202016%20Myotonic%20Annual%20Conference%20resources\">email.<\/a><\/p>\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n<\/article>\n<\/div>\n<div class=\"slideitem\">\n<article data-history-node-id=\"1437\">\n<div>\n<div id=\"accordion-1437\" class=\"accordion\">\n<div class=\"accordion-item\">\n<div id=\"node-1437\" class=\"accordion-collapse collapse show\" aria-labelledby=\"heading-1437\" data-bs-parent=\"#accordion-1437\">\n<div class=\"accordion-body\">\n<div class=\"clearfix text-formatted field field--name-body field--type-text-with-summary field--label-hidden field__item\">\n<p>Links to presentations for sessions and meetings included in the 2016 Myotonic Annual Conference Professionals Track are provided below, when available.<\/p>\n<h2>Thursday, September 15, 2016:<\/h2>\n<ul>\n<li><strong>International Physical Therapists Meeting: Defining Endpoint Measurement SOPs<\/strong>\n<ul>\n<li>Publication with the proceeds of this meeting will be published in 2017<\/li>\n<\/ul>\n<\/li>\n<li><strong>Drug Development Roundtable<\/strong>\n<ul>\n<li><strong>\u200b<\/strong>Rigor, Reproducibility and Defining Adequate Rationale for Trials (<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/DDR%20Rigor-%20Porter%20presentation%20-%20FNL%202016-09-14.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<li>Lessons Learned from Duchenne Regulatory Submissions\u00a0(<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/DDR%20Lessons%20Learned%20-%20Porter%20presentation%20-%20FNL%202016-09-14.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<li>The (Elusive) Perfect Mouse Model\u00a0(<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/DDR%20Mouse%20Elusive%20Comparison%20-%20Cooper%20presentation%20-%20FNL%202016-09-15.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<li>Feeding the Pipeline: Optimizing Academic-Industry Collaborations\u00a0(<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/DDR%20Academic%20Feeding%20the%20Pipeline%20Industry%20-%20August%20presentation%20-%20FNL%202016-09-15.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<li>Myotonic Dystrophy Burden of Disease Study Initial Findings<\/li>\n<\/ul>\n<\/li>\n<li><strong>DM Patient-Focused Drug Development (PFDD) Meeting,<\/strong>\u00a0Sheraton College Park North, Beltsville, MD\n<ul>\n<li><a href=\"https:\/\/www.myotonic.org\/digital-academy\/patient-focused-drug-development-meeting-part-1-2016-myotonic-annual-conference\" target=\"_blank\" rel=\"noopener\">Video: Patient-Focused Drug Development Meeting, Part 1 at 2016 Myotonic Annual Conference<\/a><\/li>\n<li><a href=\"https:\/\/www.myotonic.org\/digital-academy\/patient-focused-drug-development-meeting-part-2-2016-myotonic-annual-conference\" target=\"_blank\" rel=\"noopener\">Video: Patient-Focused Drug Development Meeting, Part 2 at 2016 Myotonic Annual Conference<\/a><\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<h2>Friday, September 16, 2016:<\/h2>\n<ul>\n<li><strong>Myotonic Dystrophy Clinical Research Network (DMCRN) Meeting<\/strong>\n<ul>\n<li>\u200bPresentation<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<h2>Saturday, September 17, 2016:<\/h2>\n<ul>\n<li><strong>MRI As a Research Endpoint &#8211; Grant Update<\/strong>\n<ul>\n<li>Presentation (<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/MRI%20As%20a%20Biomarker%20Endpoint-%20Lott%20presentation%20-%20FNL%202016-09-17.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<\/ul>\n<\/li>\n<li><strong>Supporting Patients: DM and Sexuality for Clinicians<\/strong>\n<ul>\n<li>Presentation\u00a0(<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/Supporting%20Patients_DM%20and%20sexuality%20for%20clinicians%20Gagnon%20FNL%202016-10-23.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<\/ul>\n<\/li>\n<li><strong>Mega Mouse: Development of a New DM Animal Model<\/strong>\n<ul>\n<li>Presentation\u00a0(<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/New%20Mouse%20Model%20-%20Porter%20presentation%20-%20FNL%202016-09-14.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<\/ul>\n<\/li>\n<li><strong>Assay and Screening Study &#8211; Grant Update<\/strong>\n<ul>\n<li>Presentation<\/li>\n<\/ul>\n<\/li>\n<li><strong>Grant Writing Training<\/strong>\n<ul>\n<li>Presentation\u00a0(<a href=\"https:\/\/www.myotonic.org\/sites\/default\/files\/event\/NIH%20Grant%20Writing%20-%20Cheever%20talk%20-%20FNL%202016-09-17.pdf\" target=\"_blank\" rel=\"noopener\">pdf<\/a>)<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<h2>Questions?<\/h2>\n<p>Contact Myotonic at\u00a0415-800-7777 or via\u00a0<a href=\"mailto:info@myotonic.org?subject=Question%20regarding%202016%20Myotonic%20Annual%20Conference%20Professional%20Track%20Session(s)\">email<\/a>.<\/p>\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n<\/article>\n<\/div>\n<\/div>\n<\/div>\n<\/article>\n<\/div>\n","protected":false},"excerpt":{"rendered":"<p>This year\u2019s MDF Annual Conference was held Thursday, September 15 &#8211; Saturday, September 17, 2016 in Washington, DC.<\/p>\n","protected":false},"featured_media":18895,"parent":0,"template":"","class_list":["post-18893","events","type-events","status-publish","has-post-thumbnail","hentry"],"_links":{"self":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/events\/18893","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/events"}],"about":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/types\/events"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/media\/18895"}],"wp:attachment":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/media?parent=18893"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}