{"id":27207,"date":"2026-08-13T08:00:17","date_gmt":"2026-08-13T15:00:17","guid":{"rendered":"https:\/\/myotonic.org\/?p=27207"},"modified":"2026-08-20T11:45:46","modified_gmt":"2026-08-20T18:45:46","slug":"congratulations-to-the-2026-spring-pilot-grant-recipients","status":"publish","type":"post","link":"https:\/\/myotonic.org\/es\/congratulations-to-the-2026-spring-pilot-grant-recipients\/","title":{"rendered":"Congratulations to the 2026 Spring Pilot Grant Recipients!"},"content":{"rendered":"

MDF’s pilot grants provide support for innovative, exploratory projects and preliminary studies to further myotonic dystrophy research. Congratulations to the 2026 Pilot Grant recipients: Dr. Jeffrey Statland, Dr. Ariadna Bargiela, and Dr. Karlien Mul!<\/p>\n

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\nJeffrey Statland, M.D.
\nUniversity of Kansas Medical Center, KS, United States <\/strong><\/p>\n

The project \u201cModeling Cardiomyopathy in DM1: A Pilot for Scalable Cardiovascular Tracking\u201d aims to improve understanding of how heart disease develops and progresses in people with DM1 by creating a shared data resource that combines electronic health record information across multiple sites. Using this data, the researchers will study how patients respond to commonly used heart treatments over time and identify factors that may predict worse outcomes or improve survival.<\/p>\n

\"\"<\/div>\n

Ariadna Bargiela, Ph.D
\nINCLIVA Health Research Institute, Valencia, Spain <\/strong><\/p>\n

The project \u201cDM2 splice index pilot study and assessment of MBNL1-modulating therapeutics\u201d aims to help prepare DM2 for future clinical trials by developing a new molecular test, the DM2 Splice Index, that can measure disease-related genetic changes in muscle cells and track whether treatments are working. The researchers will also test whether drugs already being developed for DM1, including ATX-01, currently in clinical trials for DM1, can improve these molecular abnormalities in DM2 patient-derived muscle cells.<\/p>\n

\"\"<\/div>\n

Karlien Mul, M.D., Ph.D.
\nRadboud University Medical Center (Radboudumc), Nijmegen, Netherlands <\/strong><\/p>\n

The project \u201cDM2-Activ: A Rasch-Built Patient-Reported Outcome Measure for Myotonic Dystrophy Type 2\u201d will develop DM2-Activ, a new questionnaire designed specifically to measure how DM2 affects daily functioning. Researchers across 14 centers in nine countries will collect patient-reported data online and use Rasch analysis to create a reliable, sensitive tool for use in future natural history studies and clinical trials.<\/p>\n","protected":false},"excerpt":{"rendered":"

MDF’s pilot grants provide support for innovative, exploratory projects and preliminary studies to further myotonic dystrophy research. Congratulations to the 2026 Pilot Grant recipients: Dr. Jeffrey Statland, Dr. Ariadna Bargiela, and Dr. Karlien Mul! Jeffrey Statland, M.D. University of Kansas Medical Center, KS, United States The project \u201cModeling Cardiomyopathy in DM1: A Pilot for Scalable […]<\/p>\n","protected":false},"author":13,"featured_media":0,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[70],"tags":[],"class_list":["post-27207","post","type-post","status-publish","format-standard","hentry","category-news"],"_links":{"self":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/posts\/27207","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/users\/13"}],"replies":[{"embeddable":true,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/comments?post=27207"}],"version-history":[{"count":5,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/posts\/27207\/revisions"}],"predecessor-version":[{"id":27282,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/posts\/27207\/revisions\/27282"}],"wp:attachment":[{"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/media?parent=27207"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/categories?post=27207"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/myotonic.org\/es\/wp-json\/wp\/v2\/tags?post=27207"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}