In partnership with MDF, the Wyck Foundation awarded a number of new DM research grants.
Biomarkers of various Contexts of Use are essential for drug development in DM—recent guidance documents and publications point to exciting new opportunities.
Longitudinal assessment of cognitive function in adult- and late-onset DM1 reveals a pattern of cognitive decline that can be modeled as an early-onset and acceleration of normal aging.
Thanks to the hard work and commitment of advocates from the MDF community and many others, critical legislation has moved forward that will accelerate the approval of new drugs and medical devices to treat and cure rare diseases like myotonic dystrophy.
One family was so inspired by last week’s matching gift that they’ve offered another very generous donation to keep the momentum going! Community members Rick and Paget Haylon will match the next $5,000 donated to MDF through December 10th.