Originally presented on July 2nd, 2021.

Each month biotechnology, pharmaceutical and academic partners, large and small, working on treatments and a cure for myotonic dystrophy will sit down with our community to share their progress and answer your questions. Click here to learn more about Harmony Biosciences.

Learn more about their recently announced clinical trial, Safety and Efficacy of Pitolisant on Excessive Daytime Sleepiness and Other Non-Muscular Symptoms in Patients With Myotonic Dystrophy Type 1. To view their phase 2 DM1 trial infographic, click here.

Click here to find all our upcoming Meet the DM Drug Developers dates!

Speakers include:

Medical & Clinical Team

Jeffrey Dayno, MD – Chief Medical Officer

Jeffrey M. Dayno, M.D., is the Chief Medical Officer at Harmony Biosciences. A nationally recognized expert in neuroscience, Dr. Dayno is currently responsible for leading research, development and medical and regulatory affairs for Harmony Biosciences. He is a neurologist with 10 years of experience in clinical/academic medicine, serving as Principal Investigator on numerous clinical trials, followed by over 20 years of experience in leadership roles in the pharmaceutical industry, building and leading clinical, regulatory and medical affairs teams toward multiple product approvals, with a focus over the last 10 years on drug development for rare diseases.

William Jacobson, BCMAS – Senior Director, Clinical Development

Dr. William Jacobson is the Senior Director, Clinical Development at Harmony Biosciences. Dr. Jacobson is an experienced Drug Developer and Clinical Trialist, originally trained as a Neuroscientist, with almost 30 years of experience in the Pharmaceutical industry. Dr. Jacobson works on strategic and tactical aspects of drug development and his current focus is on rare diseases of the Central Nervous System.

Patient Advocacy Team

Rachel Radomski & Kelli Wright

As the Patient Advocacy team, Rachel Radomski and Kelli Wright work with patient communities, people living with rare diseases, caregiver’s patient advocacy organizations. The Patient Advocacy team works to represent the patient perspective across Harmony and develops innovative solutions and programs to meet the dynamic needs of the communities Harmony serves. Rachel and Kelli are honored to live our core value of keeping “patients at the heart” of everything at Harmony.