MDF publishes article in therapeutic innovation and regulatory science

This publication generated by MDF, titled “Patient-Centered Therapy Development for Myotonic Dystrophy: Report of MDF–Sponsored Workshop (pdf),” was published in Therapeutic Innovation and Regulatory Science. The report examines the status of biomarker, endpoint and clinical trial design for myotonic dystrophy therapy development, and lays the groundwork for the inclusion of the patient and caregiver voice in DM therapy development. It also includes a report on the Benefits and Risks Study MDF conducted with Silicon Valley Research Group.